Trial Results

Protocol
Available Languages: English
Statistical Analysis Plan
Available Languages: English

Efficacy and Safety of ALXN1840 Administered for 48 Weeks Versus Standard of Care in Participants With Wilson Disease

Study Identifier:
WTX101-301
ClinicalTrials.gov Identifier:
EudraCT Identifier:
Sponsor:
Alexion Pharmaceuticals, Inc.
Study Contact Information:
N/A
Other

Study Details

Medical Condition
  • Unmapped
Study Drug
  • Drug: ALXN1840
  • Drug: SoC Therapy
Date
Feb 2018 - Jun 2023
Phase 1
Phase 2
Phase 3
Phase 4
N/A
Patient Requirements
Sex: Female & Male
Age: 12+ years
Requirements Information
Sex
Female & Male
Age
12+ years

Study Details

Medical Condition
  • Unmapped
Study Drug
  • Drug: ALXN1840
  • Drug: SoC Therapy
Date
Feb 2018 - Jun 2023
Phase 1
Phase 2
Phase 3
Phase 4
N/A
Patient Requirements
Sex: Female & Male
Age: 12+ years years
Requirements Information

Protocol Summary

The study will evaluate the efficacy and safety of ALXN1840 (formerly called WTX101) administered for 48 weeks compared to standard of care (SoC) in Wilson Disease (WD) participants aged 12 and older in the Primary Evaluation Period. In addition, efficacy and safety will be evaluated during an optional 60-month Extension Period.

Trial Locations

Location
Status
Location
Research Site
Los Angeles, California, United States, 90095
Status
N/A
Location
Research Site
New Haven, Connecticut, United States, 06510
Status
N/A
Location
Research Site
Chicago, Illinois, United States, 60611
Status
N/A
Location
Research Site
Ann Arbor, Michigan, United States, 48109
Status
N/A
Location
Research Site
Houston, Texas, United States, 77030
Status
N/A
Location
Research Site
Seattle, Washington, United States, 98105
Status
N/A