A Retrospective Chart Review of Deceased Patients With Mucopolysaccharidosis Type IIIB

Study Identifier:
NGLU-NH01
ClinicalTrials.gov Identifier:
EudraCT Identifier:
N/A
Sponsor:
Alexion Pharmaceuticals, Inc.
Study Contact Information:
N/A
Study Complete

Study Details

Medical Condition
  • Unmapped
Study Drug
    Date
    Jul 2013 - Jan 2015
    Phase 1
    Phase 2
    Phase 3
    Phase 4
    N/A
    Patient Requirements
    Sex: Female & Male
    Age: N/A - N/A
    Requirements Information
    Sex
    Female & Male
    Age
    N/A - N/A

    Study Details

    Medical Condition
    • Unmapped
    Study Drug
      Date
      Jul 2013 - Jan 2015
      Phase 1
      Phase 2
      Phase 3
      Phase 4
      N/A
      Patient Requirements
      Sex: Female & Male
      Age: N/A - N/A years
      Requirements Information

      Protocol Summary

      The objective is to perform a retrospective chart review to generate data to evaluate the clinical characteristics and course of disease progression of MPS IIIB.

      Trial Locations

      Location
      Status
      Location
      Pittsburg, Pennsylvania, United States
      Status
      N/A
      Location
      Porte Alegre, Brazil
      Status
      N/A
      Location
      Amsterdam, Netherlands
      Status
      N/A
      Location
      Barcelona, Spain
      Status
      N/A
      Location
      Birmingham, United Kingdom
      Status
      N/A