An Observational Study of Patients With Lysosomal Acid Lipase Deficiency/Cholesteryl Ester Storage Disease Phenotype

Study Identifier:
LAL-2-NH01
ClinicalTrials.gov Identifier:
NCT01528917
EudraCT Identifier:
N/A
Sponsor:
Alexion Pharmaceuticals, Inc.
Study Contact Information:
N/A
Study Complete

Study Details

Medical Condition
  • Unmapped
Study Drug
    Date
    Jun 2011 - Jan 2013
    Phase 1
    Phase 2
    Phase 3
    Phase 4
    N/A
    Patient Requirements
    Sex: Female & Male
    Age: 5+ years
    Requirements Information
    Sex
    Female & Male
    Age
    5+ years

    Study Details

    Medical Condition
    • Unmapped
    Study Drug
      Date
      Jun 2011 - Jan 2013
      Phase 1
      Phase 2
      Phase 3
      Phase 4
      N/A
      Patient Requirements
      Sex: Female & Male
      Age: 5+ years years
      Requirements Information

      Protocol Summary

      This is a Natural History study to characterize key aspects of the clinical course of late onset Lysosomal Acid Lipase (LAL) Deficiency/ Cholesteryl Ester Storage Disease (CESD).

      Trial Locations

      Location
      Status
      Location
      Stanford University
      Stanford, California, United States, 94305
      Status
      N/A
      Location
      Children's Memorial Hospital
      Chicago, Illinois, United States, 60614
      Status
      N/A
      Location
      University of Minnesota
      Minneapolis, Minnesota, United States, 55455
      Status
      N/A
      Location
      Morgan Stanley Children's Hospital of New York-Presbyterian
      New York, New York, United States, 10032
      Status
      N/A
      Location
      Children's Hospital of Pittsburgh
      Pittsburgh, Pennsylvania, United States, 15224
      Status
      N/A
      Location
      Seattle Children's
      Seattle, Washington, United States, 98105
      Status
      N/A